Developing Allosteric Chaperones for GBA1-Associated Disorders-An Integrated Computational and Experimental Approach

Martedì 24 dicembre 2024 ca. 1 min. di lettura

Journal and Affiliations:

International Journal of Molecular Sciences, 24 dicembre 2024

Manolo Bellotto, GT Gain Therapeutics, Lugano

Tags:
Gaucher disease
GBA1
glucocerebrosidase
lysosomal storage disease
lysosome
Parkinson’s disease
pharmacological chaperone
 
Authors:
Manolo Bellotto
Link: https://www.mdpi.com/1422-0067/26/1/9