Clinical efficacy of the enzyme replacement therapy in patients with late-onset Pompe disease: a systematic review and a meta-analysis
Martedì 13 aprile 2021
circa 1 minuti di lettura
Journal and Affiliations:
Journal of Neurology, 13 aprile 2021
Josè Vitale, Medicina intensiva, Ospedale Regionale, Mendrisio e Centro medico, Mendrisio
Alberto Pagnamenta, Medicina intensiva, Ospedale Regionale, Mendrisio e Biostatistica, Ente Ospedaliero Cantonale, Bellinzona
Tags:
enzyme replacement therapy
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gycogen storage disease type II
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late-onset pompe disease
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pompe disease
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recombinant human alpha-glucosidase
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Authors:
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Alberto Pagnamenta
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Josè Vitale
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